Blog articles

A ground-breaking new gene therapy has saved the life of its very first NHS patient
A baby girl is showing no further signs of the fatal genetic disorder metachromatic leukodystrophy after treatment with an exciting new gene therapy

What are genome editing and gene therapy?
Gene therapy and genome editing technologies are increasingly being reported on in the news and discussed in medical literature, but what are they?

Achromatopsia gene therapy partially restores children’s colour vision
A new gene therapy for achromatopsia has partially restored colour vision in two children, according to new research

NICE approves world-first MLD therapy
We explore a new gene therapy for a rare, fatal condition that affects young children

Looking back: genomics in 2021
As we approach the end of 2021, we look back on the key developments in genomics and their impact on healthcare and society

Trial underway for hATTR therapy
The novel ‘one off’ treatment could change the lives of those living with the condition

Combating cancer: POLQ inhibitors
We explore a novel treatment that could help treat cancer by preventing DNA repair in tumours

SCID gene therapy trial publishes results
This week, we look at a significant breakthrough for the treatment of severe combined immunodeficiency

Why mRNA vaccines aren't gene therapies
We bust another Covid-19 myth – this time about how mRNA vaccines work – in our latest blog post

New gene therapy launches in the UK
Baby Arthur becomes one of the first children to benefit from the landmark SMA treatment after NHS launch

New drug target identified for colorectal cancer
Around 15% of colorectal cancers are resistant to standard therapies but ‘switching off’ a specific gene could offer new avenues for treatment
News articles

New horizon-scanning webinar series for 2023
The GEP has launched the first of an exciting series of expert webinars designed to create a link between academia and genomics education