Blog articles


A baby in a blue sleep suit lies inside an incubator.

A ground-breaking new gene therapy has saved the life of its very first NHS patient

A baby girl is showing no further signs of the fatal genetic disorder metachromatic leukodystrophy after treatment with an exciting new gene therapy

What are genome editing and gene therapy?

Gene therapy and genome editing technologies are increasingly being reported on in the news and discussed in medical literature, but what are they?

Achromatopsia gene therapy partially restores children’s colour vision

A new gene therapy for achromatopsia has partially restored colour vision in two children, according to new research
Adult holding baby's hand in hospital

NICE approves world-first MLD therapy

We explore a new gene therapy for a rare, fatal condition that affects young children
Visualisation of a genome sequence as a tunnel

Looking back: genomics in 2021

As we approach the end of 2021, we look back on the key developments in genomics and their impact on healthcare and society
DNA helix with a piece separated from it in front of a light source

Trial underway for hATTR therapy

The novel ‘one off’ treatment could change the lives of those living with the condition
3D render of cancer cells

Combating cancer: POLQ inhibitors

We explore a novel treatment that could help treat cancer by preventing DNA repair in tumours

SCID gene therapy trial publishes results

This week, we look at a significant breakthrough for the treatment of severe combined immunodeficiency
Render of coronavirus, mRNA and syringe

Why mRNA vaccines aren't gene therapies

We bust another Covid-19 myth – this time about how mRNA vaccines work – in our latest blog post
Mother holding baby's hand

New gene therapy launches in the UK

Baby Arthur becomes one of the first children to benefit from the landmark SMA treatment after NHS launch
Render of a DNA helix

New drug target identified for colorectal cancer

Around 15% of colorectal cancers are resistant to standard therapies but ‘switching off’ a specific gene could offer new avenues for treatment

News articles


New horizon-scanning webinar series for 2023

The GEP has launched the first of an exciting series of expert webinars designed to create a link between academia and genomics education